Twins Undergo Gene Therapy for Progressive Muscle Condition

Initial observations indicated a gradual reduction in leg movement in the twin girls during their initial weeks. The importance of early detection and treatment from birth was emphasized due to the rapid progression of the condition.\n\n### Treatment Administered\n\nThe girls have received a one-time infusion. This treatment aims to introduce a missing gene into their bodies, with the objective of preventing further deterioration of existing muscle function. It was clarified that while the treatment can halt the progression of muscle loss, it cannot restore muscles that have already degenerated. Consequently, early intervention is considered critical for optimizing outcomes.\n\n### Post-Treatment and Prognosis\n\nFollowing the infusion, continuous physiotherapy will be required. Medical professionals have conveyed a prognosis indicating that the children are unlikely to walk or regain neck strength and will likely require wheelchairs. The mother affirmed her dedication to providing support and ensuring ongoing physiotherapy for the twins, who are experiencing this condition together.